Pastores, Gregory M.

Top Publications

Top Publications Authored or Co-Authored by "Pastores, Gregory M."

• Effect of oral eliglustat on splenomegaly in patients with Gaucher disease type 1: The ENGAGE randomized clinical trial

  JAMA - Journal of the American Medical Association, Volume 313, No. 7, Year 2015, Citations 125
• Undiagnosed Phenylketonuria Can Exist Everywhere: Results From an International Survey

  Journal of Pediatrics, Volume 239, Year 2021, Citations 100
• Multi-domain impact of elosufase alfa in Morquio A syndrome in the pivotal phase III trial

  Molecular Genetics and Metabolism, Volume 114, No. 2, Year 2015, Citations 71
• Outcomes after 18 months of eliglustat therapy in treatment-naïve adults with Gaucher disease type 1: The phase 3 ENGAGE trial

  American Journal of Hematology, Volume 92, No. 11, Year 2017, Citations 18
• Development of anti-velaglucerase alfa antibodies in clinical trial-treated patients with Gaucher disease

  Blood Cells, Molecules, and Diseases, Volume 59, Year 2016, Citations 9