Schmidt, Manfred C.

Top Publications

Top Publications Authored or Co-Authored by "Schmidt, Manfred C."

• Gene therapy for Wiskott-Aldrich syndrome-long-term efficacy and genotoxicity

  Science Translational Medicine, Volume 6, No. 227, Article 227ra33, Year 2014, Citations 465
• Oncogenesis following delivery of a nonprimate lentiviral gene therapy vector to fetal and neonatal mice

  Molecular Therapy, Volume 12, No. 4, Year 2005, Citations 224
• Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaques

  Molecular Therapy, Volume 19, No. 11, Year 2011, Citations 54
• In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model

  Molecular Therapy, Volume 25, No. 8, Year 2017, Citations 28
• The fetal mouse is a sensitive genotoxicity model that exposes lentiviral-associated mutagenesis resulting in liver oncogenesis

  Molecular Therapy, Volume 21, No. 2, Year 2013, Citations 27