Johana, Nuryanti Binti

Top Publications

Top Publications Authored or Co-Authored by "Johana, Nuryanti Binti"

• Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaques

  Molecular Therapy, Volume 19, No. 11, Year 2011, Citations 54
• Systemic delivery of scAAV9 in fetal macaques facilitates neuronal transduction of the central and peripheral nervous systems

  Gene Therapy, Volume 20, No. 1, Year 2013, Citations 42
• In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model

  Molecular Therapy, Volume 25, No. 8, Year 2017, Citations 28
• Therapeutic expression of human clotting factors IX and × following adeno-associated viral vector-mediated intrauterine gene transfer in early-gestation fetal macaques

  FASEB Journal, Volume 33, No. 3, Year 2019, Citations 18
• A comparison of intrauterine hemopoietic cell transplantation and lentiviral gene transfer for the correction of severe β-thalassemia in a HbbTh3/+ murine model

  Experimental Hematology, Volume 62, Year 2018, Citations 14