Nathwani, Amit Chunilal

Top Publications

Top Publications Authored or Co-Authored by "Nathwani, Amit Chunilal"

• Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver

  Blood, Volume 107, No. 7, Year 2006, Citations 336
• Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins

  Molecular Therapy, Volume 19, No. 5, Year 2011, Citations 280
• Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant

  Blood, Volume 121, No. 17, Year 2013, Citations 218
• Codon optimization of human factor VIII cDNAs leads to high-level expression

  Blood, Volume 117, No. 3, Year 2011, Citations 142
• Polymorphic sites in the African population detected by sequence analysis of the glucose-6-phosphate dehydrogenase gene outline the evolution of the variants A and A-

  Proceedings of the National Academy of Sciences of the United States of America, Volume 88, No. 19, Year 1991, Citations 82